Etienne Sokal

Catholic University of Louvain (UCL) - Cliniques Universitaires Saint-Luc

Belgium

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Scholarly Papers (1)

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Maralixibat Treatment Significantly Reduces Pruritus and Serum Bile Acids in Patients with Alagille Syndrome: Results from a Randomized Phase II Study with 4 Years of Follow-Up

Number of pages: 37 Posted: 26 Jan 2021
Hépatologie et Transplantation Hépatique Pédiatriques, Hôpital Bicêtre, AP-HP, Université Paris-Saclay, Department of Gastroenterology, The Royal Children’s Hospital Melbourne, Department of Gastroenterology, The Children’s Hospital at Westmead, Department of Child Health, The Paediatric Liver Centre, King’s College Hospital, Hospital Universitario La Paz - Department of Paediatric Hepatology and Liver Transplantation, Department of Gastroenterology, Hepatology, Feeding Disorders and Pediatrics, Children's Memorial Health Institute, Gastroenterology-Hepatology-Nutrition Unit, Hôpital Universitaire Necker-Enfants Malades, Service de Gastroentérologie, Hépatologie et Nutrition Pédiatriques, Hôpital Femme-Mère-Enfant, Paediatric Gastroenterology/Hepatology, University Hospital for Children and Adolescents, Cincinnati Children's Hospital Medical Center, Amplyx Pharmaceuticals, Stanford Medical School, Stanford University, Biostatistics, Premier Research, Takeda Pharmaceuticals, Mirum Pharmaceuticals, Mirum Pharmaceuticals, Mirum Pharmaceuticals, Catholic University of Louvain (UCL) - Cliniques Universitaires Saint-Luc and Hépatologie et Transplantation Hépatique Pédiatriques, Hôpital Bicêtre, AP-HP, Université Paris-Saclay
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Abstract:

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Serum bile acids, pruritus, liver disease, Alagille syndrome, cholestasis, maralixibat, apical sodium-dependent bile acid transporter