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Elizabeth J. Meiman

University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory

SCHOLARLY PAPERS

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Scholarly Papers (1)

1.

Intravitreal Gene Therapy Preserves Retinal Function in a Canine Model of CLN2 Neuronal Ceroid Lipofuscinosis

Number of pages: 50 Posted: 22 Sep 2022
University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory, University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory, University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory, University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory, University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory, University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory, University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory, University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory and University of Missouri at Columbia - Neurodegenerative Diseases Research Laboratory
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Abstract:

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lysosomal storage disease, retinal degeneration, Batten disease, tripeptidyl peptidase, electroretinogram, ocular gene therapy