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Lucinda Carr

Great Ormond Street Hospital

SCHOLARLY PAPERS

1

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54

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0

Scholarly Papers (1)

1.

Therapeutic Activity of a Haematopoietic Stem Cell-Delivered Tissue-Penetrating Peptide in Friedreich's Ataxia Models

Number of pages: 37 Posted: 21 Nov 2024
Brunel University London, Brunel University London, University College London, University College London, University College London, University College London, Brunel University London, Brunel University London, Great Ormond Street Hospital, Great Ormond Street Hospital - Department of Paediatric Infectious Diseases, Great Ormond Street Hospital, University College London, University College London, Brunel University London and Independent
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Abstract:

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Gene therapy, Friedreich's ataxia, cell penetrating peptide, neurodegneration, autologous transplantation