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Jens O. Watzlawik

Mayo Clinic

SCHOLARLY PAPERS

1

DOWNLOADS

43

TOTAL CITATIONS

0

Scholarly Papers (1)

1.

N-of-1 CHCHD10 ALS Antisense Oligonucleotide Trial Shows Early Signs of Efficacy

Number of pages: 6 Posted: 25 Jul 2025
Mayo Clinic, Orlando Health, n-Lorem Foundation, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Emory University, Mayo Clinic - Florida and Mayo Clinic
Downloads 43 (1,145,108)

Abstract:

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Amyotrophic lateral sclerosis, Antisense oligonucleotide, CHCHD10, Neurofilament light