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Jens O. Watzlawik
Mayo Clinic
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SCHOLARLY PAPERS
1
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43
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Scholarly Papers (1)
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1.
N-of-1 CHCHD10 ALS Antisense Oligonucleotide Trial Shows Early Signs of Efficacy
Number of pages: 6
Posted: 25 Jul 2025
Margot A. Cousin
,
Aditi I. Dagli
,
Laurence Mignon
,
Jaimin S. Shah
,
Mercedes Prudencio
,
Tania F. Gendron
,
Marka Van Blitterswijk
,
Erik H. Middlebrooks
,
Megan Donahue
,
Jany Dagher
, Jens O. Watzlawik,
Wolfdieter Springer
,
Zachary McEachin
,
Leonard Petrucelli
and
Bjorn Oskarsson
Mayo Clinic, Orlando Health, n-Lorem Foundation, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Mayo Clinic, Emory University, Mayo Clinic - Florida and Mayo Clinic
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Abstract:
Amyotrophic lateral sclerosis, Antisense oligonucleotide, CHCHD10, Neurofilament light
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