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Ravi Savarirayan

University of Melbourne - Murdoch Children's Research Institute

SCHOLARLY PAPERS

2

DOWNLOADS

159

TOTAL CITATIONS

0

Scholarly Papers (2)

1.

Once-Weekly TransCon CNP in Children with Achondroplasia (ACcomplisH): A Phase 2, Multicentre, Randomised, Double-Blind, Placebo-Controlled, Dose-Escalation Trial

Number of pages: 29 Posted: 27 Jun 2023
University of Melbourne - Murdoch Children's Research Institute, University of Missouri Children’s Hospital, Copenhagen University College - Hospital Rigshospitalet, University of Arkansas for Medical Sciences, Baylor College of Medicine, Nemours Children's Hospital, University of Wisconsin-Madison - School of Medicine and Public Health, Johannes Kepler University Linz, State University of New York (SUNY) - University at Buffalo, Children’s Minnesota, University of Auckland - The Liggins Institute, Children's Hospital Colorado, Children's Hospital Colorado, Charité - Universitätsmedizin Berlin - Center for Chronically Sick Children, Hospital Pediátrico de Coimbra, Ascendis Pharma Inc., Ascendis Pharma Inc., Ascendis Pharma Inc., Ascendis Pharma Inc., Ascendis Pharma A/S, Ascendis Pharma A/S, Ascendis Pharma Inc. and Children’s Health Ireland
Downloads 134 (551,165)

Abstract:

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Achondroplasia, C-type Natriuretic Peptide, growth, TransCon CNP, Paediatric

2.

Sustained Growth-Promoting Effects of Vosoritide in Children with Achondroplasia from an Ongoing Phase 3 Extension Study

Number of pages: 31 Posted: 13 Aug 2024
University of Melbourne - Murdoch Children's Research Institute, Guy's and St Thomas' NHS Foundation Trust - Evelina London Children's Hospital, Emory University - School of Medicine, Baylor College of Medicine, Johns Hopkins University - School of Medicine, University of California, San Francisco (UCSF) - Benioff Children's Hospital, The Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, Otto-von-Guericke-Universität Magdeburg, Ann & Robert H. Lurie Children’s Hospital of Chicago, The University of Osaka - Graduate School of Medicine, Sheffield Children's NHS Foundation Trust - Highly Specialised Osteogenesis Imperfecta Service, Tokushima University, Hospital Universitario Virgen de la Victoria, Nemours/Alfred I. duPont Hospital for Children, University of Texas at Houston - McGovern Medical School, University of Wisconsin-Madison - School of Medicine and Public Health, BioMarin (UK) Limited, Ltd., BioMarin (UK) Limited, Ltd., BioMarin (UK) Limited, Ltd., BioMarin (UK) Limited, Ltd. and BioMarin (UK) Limited, Ltd.
Downloads 25 (1,385,945)

Abstract:

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Achondroplasia, vosoritide, annualized growth velocity, body proportionality