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Maria Pia Cicalese

Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele

Milano

Italy

SCHOLARLY PAPERS

2

DOWNLOADS

233

TOTAL CITATIONS

0

Scholarly Papers (2)

1.

Long-Term Outcome in Wiskott-Aldrich Syndrome and X-Linked Thrombocytopenia Patients: A Retrospective-Prospective Multi-Center Study of the Italian Primary Immune Deficiency Network (IPINET)

Number of pages: 25 Posted: 07 Jul 2024
University of Brescia - Department of Clinical and Experimental Sciences, University of Bologna, University of Brescia - Spedali Civili, Bambino Gesù Children's Hospital - Department of Pediatric Hematology and Oncology, Università Vita-Salute San Raffaele - San Raffaele Hospital, University of Padova, IRCCS “Burlo Garofolo”, Federico II University, Santobono-Pausilipon Children's Hospital, IRCCS Azienda Ospedaliero-Universitaria di Bologna, IRCCS Istituto Giannina Gaslini, University of Milano - Bicocca, University of Bologna, University of Antioquia - IPS Universitaria, University of Florence - Immunology Unit, University of Tor Vergata, Fondazione IRCCS Policlinico San Matteo - Pediatric Hematology/Oncology and Cell Factory, Università Vita-Salute San Raffaele - San Raffaele Hospital, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, San Giovanni di Dio Ruggi d'Aragona, University of Brescia, Ospedale Dimiccoli Barletta, University of Brescia - Department of Molecular and Translational Medicine, University of Brescia, ASST-Spedali Civili of Brescia, University of Brescia, National Institute of Allergy and Infectious Diseases, IRCCS Azienda Ospedaliero-Universitaria di Bologna, University of Brescia - Department of Clinical and Experimental Sciences and affiliation not provided to SSRN
Downloads 119 (600,462)

Abstract:

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Primary immunodeficiency, Wiskott-Aldrich syndrome, thrombocytopenia, bone marrow transplantation, gene therapy

2.

Early Bone Marrow Alterations in Patients with Adenosine Deaminase 2 Deficiency Across Disease Phenotypes and Severities

Number of pages: 29 Posted: 18 Apr 2024
Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute, Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute, Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute, Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute, Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute, UOSD Centro Malattie Autoinfiammatorie ed Immunodeficienze, IRCCS Istituto Giannina Gaslini, IRCCS Istituto Giannina Gaslini, IRCCS Istituto Giannina Gaslini, IRCCS Istituto Giannina Gaslini, IRCCS Istituto Giannina Gaslini, IRCCS Istituto Giannina Gaslini, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, Bambino Gesù Children's Hospital, Bambino Gesù Children's Hospital, Sapienza University of Rome - IRCCS Ospedale Pediatrico Bambino Gesù, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, Regione Emilia-Romagna - IRCCS Azienda Ospedaliero-Universitaria di Bologna, IRCCS Istituto Giannina Gaslini, IRCCS Istituto Giannina Gaslini, IRCCS Istituto Giannina Gaslini, Università Vita-Salute San Raffaele - San Raffaele Hospital and Università Vita-Salute San Raffaele - IRCCS San Raffaele Scientific Institute
Downloads 114 (621,896)

Abstract:

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adenosine deaminase 2 deficiency, bone marrow, bone marrow failure, cytopenia, hematopoietic stem cell transplantation, mesenchymal stroma cells, senescence