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ASST-Spedali Civili of Brescia

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Scholarly Papers (1)

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Long-Term Outcome in Wiskott-Aldrich Syndrome and X-Linked Thrombocytopenia Patients: A Retrospective-Prospective Multi-Center Study of the Italian Primary Immune Deficiency Network (IPINET)

Number of pages: 25 Posted: 07 Jul 2024
University of Brescia - Department of Clinical and Experimental Sciences, University of Bologna, University of Brescia - Spedali Civili, Bambino Gesù Children's Hospital - Department of Pediatric Hematology and Oncology, Università Vita-Salute San Raffaele - San Raffaele Hospital, University of Padova, IRCCS “Burlo Garofolo”, Federico II University, Santobono-Pausilipon Children's Hospital, IRCCS Azienda Ospedaliero-Universitaria di Bologna, IRCCS Istituto Giannina Gaslini, University of Milano - Bicocca, University of Bologna, University of Antioquia - IPS Universitaria, University of Florence - Immunology Unit, University of Tor Vergata, Fondazione IRCCS Policlinico San Matteo - Pediatric Hematology/Oncology and Cell Factory, Università Vita-Salute San Raffaele - San Raffaele Hospital, Università Vita-Salute San Raffaele - IRCCS Ospedale San Raffaele, San Giovanni di Dio Ruggi d'Aragona, University of Brescia, Ospedale Dimiccoli Barletta, University of Brescia - Department of Molecular and Translational Medicine, University of Brescia, ASST-Spedali Civili of Brescia, University of Brescia, National Institute of Allergy and Infectious Diseases, IRCCS Azienda Ospedaliero-Universitaria di Bologna, University of Brescia - Department of Clinical and Experimental Sciences and affiliation not provided to SSRN
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Abstract:

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Primary immunodeficiency, Wiskott-Aldrich syndrome, thrombocytopenia, bone marrow transplantation, gene therapy