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Rainald Fischer

Ionis Pharmaceuticals

United States

SCHOLARLY PAPERS

1

DOWNLOADS

123

TOTAL CITATIONS

4

Scholarly Papers (1)

1.

Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Single and Multiple Doses of ION-827359, an Antisense Oligonucleotide Inhibitor of ENaC, in Healthy Volunteers and Patients with Cystic Fibrosis: A Double-Blind, Placebo-Controlled, Dose-Escalation, Phase 1/2a Study

Number of pages: 30 Posted: 20 Apr 2022
University of Duisburg-Essen - Division of Cystic Fibrosis, Ionis Pharmaceuticals, Ionis Pharmaceuticals, The University of Manchester - Wythenshawe Hospital, Ionis Pharmaceuticals, Ionis Pharmaceuticals, Ionis Pharmaceuticals, Ionis Pharmaceuticals and Queen’s University Belfast - Department of Medicine, Health and Life Sciences
Downloads 123 (588,531)
Citation 4

Abstract:

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cystic fibrosis, epithelial sodium channels, pharmacokinetics, safety, forced expiratory volume in 1 second, ION-827359